{"id":398939,"date":"2025-05-12T14:05:00","date_gmt":"2025-05-12T12:05:00","guid":{"rendered":"https:\/\/medizinonline.com\/?p=398939"},"modified":"2025-05-12T14:25:04","modified_gmt":"2025-05-12T12:25:04","slug":"stargardts-disease-groundbreaking-gene-therapy-study-gives-hope","status":"publish","type":"post","link":"https:\/\/medizinonline.com\/en\/stargardts-disease-groundbreaking-gene-therapy-study-gives-hope\/","title":{"rendered":"Stargardt&#8217;s disease: groundbreaking gene therapy study gives hope"},"content":{"rendered":"\n<p class=\"wp-block-paragraph\"><strong>In Stargardt disease, loss-of-function mutations in the ABCA4 gene lead to macular degeneration and blindness. A team led by researchers from the University of Basel has developed a promising new therapeutic approach. In their study, they were able to demonstrate precise gene correction using &#8220;base editing&#8221;. The results were published in the journal <em>Nature Medicine<\/em>.   <\/strong><\/p>\n\n<div class=\"pmpro\"><div class=\"pmpro_card pmpro_content_message\"><div class=\"pmpro_card_content\">Dieser Inhalt ist nur f\u00fcr Benutzer der Gruppe: Medizinische Fachperson zug\u00e4nglich <br \/><a href=\"https:\/\/medizinonline.com\/en\/my-account\/packages\/\">Jetzt beitreten<\/a><\/div><div class=\"pmpro_card_actions pmpro_font-medium\">Already a member? <a href=\"https:\/\/medizinonline.com\/en\/log-in\/?redirect_to=https%3A%2F%2Fmedizinonline.com%2Fen%2Fstargardts-disease-groundbreaking-gene-therapy-study-gives-hope%2F\">Log in here<\/a><\/div><\/div><\/div>","protected":false},"excerpt":{"rendered":"<p>In Stargardt disease, loss-of-function mutations in the ABCA4 gene lead to macular degeneration and blindness. A team led by researchers from the University of Basel has developed a promising new&#8230;&hellip;... <\/p>\n<div class=\"pmpro\"><div class=\"pmpro_card pmpro_content_message\"><div class=\"pmpro_card_content\">Dieser Inhalt ist nur f\u00fcr Benutzer der Gruppe: Medizinische Fachperson zug\u00e4nglich <br \/><a href=\"https:\/\/medizinonline.com\/en\/my-account\/packages\/\">Jetzt beitreten<\/a><\/div><div class=\"pmpro_card_actions pmpro_font-medium\">Already a member? <a href=\"https:\/\/medizinonline.com\/en\/log-in\/?redirect_to=https%3A%2F%2Fmedizinonline.com%2Fen%2Fstargardts-disease-groundbreaking-gene-therapy-study-gives-hope%2F\">Log in here<\/a><\/div><\/div><\/div>","protected":false},"author":7,"featured_media":398942,"comment_status":"closed","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"_acf_changed":false,"pmpro_default_level":"","cat_1_feature_home_top":false,"cat_2_editor_pick":false,"csco_eyebrow_text":"Journal Club","footnotes":""},"category":[11508,11297,11396,11423,11548,11503],"tags":[64126,27081,82282],"powerkit_post_featured":[],"class_list":["post-398939","post","type-post","status-publish","format-standard","has-post-thumbnail","category-education","category-general-internal-medicine","category-genetics","category-ophthalmology","category-rx-en","category-studies","tag-blindness","tag-macular-degeneration","tag-stargardts-disease","pmpro-level-required","pmpro-level-1","pmpro-no-access"],"acf":[],"publishpress_future_action":{"enabled":false,"date":"2026-07-09 22:23:01","action":"change-status","newStatus":"draft","terms":[],"taxonomy":"category","extraData":[]},"publishpress_future_workflow_manual_trigger":{"enabledWorkflows":[]},"wpml_current_locale":"en_US","wpml_translations":{"fr_FR":{"locale":"fr_FR","id":398756,"slug":"maladie-de-stargardt-une-etude-de-therapie-genique-pionniere-donne-de-lespoir","post_title":"Maladie de Stargardt : une \u00e9tude de th\u00e9rapie g\u00e9nique pionni\u00e8re donne de l'espoir","href":"https:\/\/medizinonline.com\/fr\/maladie-de-stargardt-une-etude-de-therapie-genique-pionniere-donne-de-lespoir\/"},"it_IT":{"locale":"it_IT","id":398768,"slug":"malattia-di-stargardt-un-innovativo-studio-di-terapia-genica-da-speranza","post_title":"Malattia di Stargardt: un innovativo studio di terapia genica d\u00e0 speranza","href":"https:\/\/medizinonline.com\/it\/malattia-di-stargardt-un-innovativo-studio-di-terapia-genica-da-speranza\/"},"pt_PT":{"locale":"pt_PT","id":398775,"slug":"doenca-de-stargardt-estudo-inovador-de-terapia-genetica-da-esperanca","post_title":"Doen\u00e7a de Stargardt: estudo inovador de terapia gen\u00e9tica d\u00e1 esperan\u00e7a","href":"https:\/\/medizinonline.com\/pt-pt\/doenca-de-stargardt-estudo-inovador-de-terapia-genetica-da-esperanca\/"},"es_ES":{"locale":"es_ES","id":398754,"slug":"enfermedad-de-stargardt-un-innovador-estudio-de-terapia-genica-da-esperanzas","post_title":"Enfermedad de Stargardt: un innovador estudio de terapia g\u00e9nica da esperanzas","href":"https:\/\/medizinonline.com\/es\/enfermedad-de-stargardt-un-innovador-estudio-de-terapia-genica-da-esperanzas\/"}},"_links":{"self":[{"href":"https:\/\/medizinonline.com\/en\/wp-json\/wp\/v2\/posts\/398939","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/medizinonline.com\/en\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/medizinonline.com\/en\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/medizinonline.com\/en\/wp-json\/wp\/v2\/users\/7"}],"replies":[{"embeddable":true,"href":"https:\/\/medizinonline.com\/en\/wp-json\/wp\/v2\/comments?post=398939"}],"version-history":[{"count":1,"href":"https:\/\/medizinonline.com\/en\/wp-json\/wp\/v2\/posts\/398939\/revisions"}],"predecessor-version":[{"id":398943,"href":"https:\/\/medizinonline.com\/en\/wp-json\/wp\/v2\/posts\/398939\/revisions\/398943"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/medizinonline.com\/en\/wp-json\/wp\/v2\/media\/398942"}],"wp:attachment":[{"href":"https:\/\/medizinonline.com\/en\/wp-json\/wp\/v2\/media?parent=398939"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/medizinonline.com\/en\/wp-json\/wp\/v2\/category?post=398939"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/medizinonline.com\/en\/wp-json\/wp\/v2\/tags?post=398939"},{"taxonomy":"powerkit_post_featured","embeddable":true,"href":"https:\/\/medizinonline.com\/en\/wp-json\/wp\/v2\/powerkit_post_featured?post=398939"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}