{"id":398754,"date":"2025-05-12T14:05:00","date_gmt":"2025-05-12T12:05:00","guid":{"rendered":"https:\/\/medizinonline.com\/?p=398754"},"modified":"2025-05-12T14:25:08","modified_gmt":"2025-05-12T12:25:08","slug":"enfermedad-de-stargardt-un-innovador-estudio-de-terapia-genica-da-esperanzas","status":"publish","type":"post","link":"https:\/\/medizinonline.com\/es\/enfermedad-de-stargardt-un-innovador-estudio-de-terapia-genica-da-esperanzas\/","title":{"rendered":"Enfermedad de Stargardt: un innovador estudio de terapia g\u00e9nica da esperanzas"},"content":{"rendered":"\n<p><strong>En la enfermedad de Stargardt, las mutaciones de p\u00e9rdida de funci\u00f3n en el gen ABCA4 provocan degeneraci\u00f3n macular y ceguera. Un equipo dirigido por investigadores de la Universidad de Basilea ha desarrollado un nuevo y prometedor enfoque terap\u00e9utico. En su estudio, pudieron demostrar la correcci\u00f3n precisa del gen mediante la &#8220;edici\u00f3n de bases&#8221;. Los resultados se publicaron en la revista <em>Nature Medicine<\/em>.   <\/strong><\/p>\n\n<div class=\"pmpro\"><div class=\"pmpro_card pmpro_content_message\"><div class=\"pmpro_card_content\">Dieser Inhalt ist nur f\u00fcr Benutzer der Gruppe: Medizinische Fachperson zug\u00e4nglich <br \/><a href=\"https:\/\/medizinonline.com\/es\/mi-cuenta\/paquetes\/\">Jetzt beitreten<\/a><\/div><div class=\"pmpro_card_actions pmpro_font-medium\">\u00bfYa eres miembro? <a href=\"https:\/\/medizinonline.com\/es\/conectarse\/?redirect_to=https%3A%2F%2Fmedizinonline.com%2Fes%2Fenfermedad-de-stargardt-un-innovador-estudio-de-terapia-genica-da-esperanzas%2F\">Accede aqu\u00ed<\/a><\/div><\/div><\/div>","protected":false},"excerpt":{"rendered":"<p>En la enfermedad de Stargardt, las mutaciones de p\u00e9rdida de funci\u00f3n en el gen ABCA4 provocan degeneraci\u00f3n macular y ceguera. Un equipo dirigido por investigadores de la Universidad de Basilea&#8230;&hellip;... <\/p>\n<div class=\"pmpro\"><div class=\"pmpro_card pmpro_content_message\"><div class=\"pmpro_card_content\">Dieser Inhalt ist nur f\u00fcr Benutzer der Gruppe: Medizinische Fachperson zug\u00e4nglich <br \/><a href=\"https:\/\/medizinonline.com\/es\/mi-cuenta\/paquetes\/\">Jetzt beitreten<\/a><\/div><div class=\"pmpro_card_actions pmpro_font-medium\">\u00bfYa eres miembro? <a href=\"https:\/\/medizinonline.com\/es\/conectarse\/?redirect_to=https%3A%2F%2Fmedizinonline.com%2Fes%2Fenfermedad-de-stargardt-un-innovador-estudio-de-terapia-genica-da-esperanzas%2F\">Accede aqu\u00ed<\/a><\/div><\/div><\/div>","protected":false},"author":7,"featured_media":398761,"comment_status":"closed","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"_acf_changed":false,"pmpro_default_level":"","cat_1_feature_home_top":false,"cat_2_editor_pick":false,"csco_eyebrow_text":"Journal Club","footnotes":""},"category":[11475,11478,11364,11288,11386,11552],"tags":[82174,27160,82173],"powerkit_post_featured":[],"class_list":["post-398754","post","type-post","status-publish","format-standard","has-post-thumbnail","category-estudios","category-formacion-continua","category-genetica","category-medicina-interna-general","category-oftalmologia","category-rx-es","tag-ceguera-es","tag-degeneracion-macular","tag-enfermedad-de-stargardt","pmpro-level-required","pmpro-level-1","pmpro-no-access"],"acf":[],"publishpress_future_action":{"enabled":false,"date":"2026-05-04 04:17:35","action":"change-status","newStatus":"draft","terms":[],"taxonomy":"category","extraData":[]},"publishpress_future_workflow_manual_trigger":{"enabledWorkflows":[]},"wpml_current_locale":"es_ES","wpml_translations":[],"_links":{"self":[{"href":"https:\/\/medizinonline.com\/es\/wp-json\/wp\/v2\/posts\/398754","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/medizinonline.com\/es\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/medizinonline.com\/es\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/medizinonline.com\/es\/wp-json\/wp\/v2\/users\/7"}],"replies":[{"embeddable":true,"href":"https:\/\/medizinonline.com\/es\/wp-json\/wp\/v2\/comments?post=398754"}],"version-history":[{"count":1,"href":"https:\/\/medizinonline.com\/es\/wp-json\/wp\/v2\/posts\/398754\/revisions"}],"predecessor-version":[{"id":398765,"href":"https:\/\/medizinonline.com\/es\/wp-json\/wp\/v2\/posts\/398754\/revisions\/398765"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/medizinonline.com\/es\/wp-json\/wp\/v2\/media\/398761"}],"wp:attachment":[{"href":"https:\/\/medizinonline.com\/es\/wp-json\/wp\/v2\/media?parent=398754"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/medizinonline.com\/es\/wp-json\/wp\/v2\/category?post=398754"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/medizinonline.com\/es\/wp-json\/wp\/v2\/tags?post=398754"},{"taxonomy":"powerkit_post_featured","embeddable":true,"href":"https:\/\/medizinonline.com\/es\/wp-json\/wp\/v2\/powerkit_post_featured?post=398754"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}