{"id":410340,"date":"2025-11-20T00:30:00","date_gmt":"2025-11-19T23:30:00","guid":{"rendered":"https:\/\/medizinonline.com\/?p=410340"},"modified":"2025-10-23T14:41:41","modified_gmt":"2025-10-23T12:41:41","slug":"datos-a-largo-plazo-sobre-los-moduladores-del-cftr-en-ninos-con-fibrosis-quistica","status":"publish","type":"post","link":"https:\/\/medizinonline.com\/es\/datos-a-largo-plazo-sobre-los-moduladores-del-cftr-en-ninos-con-fibrosis-quistica\/","title":{"rendered":"Datos a largo plazo sobre los moduladores del CFTR en ni\u00f1os con fibrosis qu\u00edstica"},"content":{"rendered":"\n<p><strong>La fibrosis qu\u00edstica (FQ) es una de las enfermedades metab\u00f3licas cong\u00e9nitas m\u00e1s comunes en Europa. Las opciones de tratamiento para los enfermos de FQ se han ampliado considerablemente en los \u00faltimos a\u00f1os. Los moduladores del CFTR mejoran la funci\u00f3n de la prote\u00edna CFTR defectuosa y son, por tanto, los primeros f\u00e1rmacos con un efecto causal al menos parcial en la FQ. En un estudio de extensi\u00f3n de fase IIIb abierto, se investig\u00f3 el uso de la terapia combinada de ivacaftor, elexacaftor y tezacaftor en ni\u00f1os de 6 a 11 a\u00f1os durante un periodo de 96 semanas.   <\/strong><\/p>\n\n<div class=\"pmpro\"><div class=\"pmpro_card pmpro_content_message\"><div class=\"pmpro_card_content\">Dieser Inhalt ist nur f\u00fcr Benutzer der Gruppe: Medizinische Fachperson zug\u00e4nglich <br \/><a href=\"https:\/\/medizinonline.com\/es\/mi-cuenta\/paquetes\/\">Jetzt beitreten<\/a><\/div><div class=\"pmpro_card_actions pmpro_font-medium\">\u00bfYa eres miembro? <a href=\"https:\/\/medizinonline.com\/es\/conectarse\/?redirect_to=https%3A%2F%2Fmedizinonline.com%2Fes%2Fdatos-a-largo-plazo-sobre-los-moduladores-del-cftr-en-ninos-con-fibrosis-quistica%2F\">Accede aqu\u00ed<\/a><\/div><\/div><\/div>","protected":false},"excerpt":{"rendered":"<p>La fibrosis qu\u00edstica (FQ) es una de las enfermedades metab\u00f3licas cong\u00e9nitas m\u00e1s comunes en Europa. Las opciones de tratamiento para los enfermos de FQ se han ampliado considerablemente en los&#8230;&hellip;... <\/p>\n<div class=\"pmpro\"><div class=\"pmpro_card pmpro_content_message\"><div class=\"pmpro_card_content\">Dieser Inhalt ist nur f\u00fcr Benutzer der Gruppe: Medizinische Fachperson zug\u00e4nglich <br \/><a href=\"https:\/\/medizinonline.com\/es\/mi-cuenta\/paquetes\/\">Jetzt beitreten<\/a><\/div><div class=\"pmpro_card_actions pmpro_font-medium\">\u00bfYa eres miembro? <a href=\"https:\/\/medizinonline.com\/es\/conectarse\/?redirect_to=https%3A%2F%2Fmedizinonline.com%2Fes%2Fdatos-a-largo-plazo-sobre-los-moduladores-del-cftr-en-ninos-con-fibrosis-quistica%2F\">Accede aqu\u00ed<\/a><\/div><\/div><\/div>","protected":false},"author":7,"featured_media":410342,"comment_status":"closed","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"_acf_changed":false,"pmpro_default_level":"","cat_1_feature_home_top":false,"cat_2_editor_pick":false,"csco_eyebrow_text":"Informe del estudio","footnotes":""},"category":[11475,11478,11288,11424,11402,11552],"tags":[15522,83337,21410,83336,12211,83338],"powerkit_post_featured":[],"class_list":["post-410340","post","type-post","status-publish","format-standard","has-post-thumbnail","category-estudios","category-formacion-continua","category-medicina-interna-general","category-neumologia","category-pediatria","category-rx-es","tag-cf-es","tag-elexacaftor-es","tag-fibrosis-quistica-es-2","tag-ivacaftor-es","tag-moduladores-cftr-es","tag-tezacaftor-es","pmpro-level-required","pmpro-level-1","pmpro-no-access"],"acf":[],"publishpress_future_action":{"enabled":false,"date":"2026-04-11 01:34:21","action":"change-status","newStatus":"draft","terms":[],"taxonomy":"category","extraData":[]},"publishpress_future_workflow_manual_trigger":{"enabledWorkflows":[]},"wpml_current_locale":"es_ES","wpml_translations":[],"_links":{"self":[{"href":"https:\/\/medizinonline.com\/es\/wp-json\/wp\/v2\/posts\/410340","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/medizinonline.com\/es\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/medizinonline.com\/es\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/medizinonline.com\/es\/wp-json\/wp\/v2\/users\/7"}],"replies":[{"embeddable":true,"href":"https:\/\/medizinonline.com\/es\/wp-json\/wp\/v2\/comments?post=410340"}],"version-history":[{"count":1,"href":"https:\/\/medizinonline.com\/es\/wp-json\/wp\/v2\/posts\/410340\/revisions"}],"predecessor-version":[{"id":410343,"href":"https:\/\/medizinonline.com\/es\/wp-json\/wp\/v2\/posts\/410340\/revisions\/410343"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/medizinonline.com\/es\/wp-json\/wp\/v2\/media\/410342"}],"wp:attachment":[{"href":"https:\/\/medizinonline.com\/es\/wp-json\/wp\/v2\/media?parent=410340"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/medizinonline.com\/es\/wp-json\/wp\/v2\/category?post=410340"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/medizinonline.com\/es\/wp-json\/wp\/v2\/tags?post=410340"},{"taxonomy":"powerkit_post_featured","embeddable":true,"href":"https:\/\/medizinonline.com\/es\/wp-json\/wp\/v2\/powerkit_post_featured?post=410340"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}