{"id":410403,"date":"2025-11-20T00:30:00","date_gmt":"2025-11-19T23:30:00","guid":{"rendered":"https:\/\/medizinonline.com\/?p=410403"},"modified":"2025-10-23T14:42:31","modified_gmt":"2025-10-23T12:42:31","slug":"dati-a-lungo-termine-sui-modulatori-cftr-nei-bambini-con-fibrosi-cistica","status":"publish","type":"post","link":"https:\/\/medizinonline.com\/it\/dati-a-lungo-termine-sui-modulatori-cftr-nei-bambini-con-fibrosi-cistica\/","title":{"rendered":"Dati a lungo termine sui modulatori CFTR nei bambini con fibrosi cistica"},"content":{"rendered":"\n<p><strong>La fibrosi cistica (FC) \u00e8 una delle malattie metaboliche congenite pi\u00f9 comuni in Europa. Le opzioni di trattamento per le persone affette da FC sono aumentate in modo significativo negli ultimi anni. I modulatori CFTR migliorano la funzione della proteina CFTR difettosa e sono quindi i primi farmaci con un effetto causale almeno parziale nella FC. In uno studio di estensione di fase IIIb in aperto, l&#8217;uso della terapia combinata di ivacaftor, elexacaftor e tezacaftor \u00e8 stato studiato in bambini di 6-11 anni per un periodo di 96 settimane.   <\/strong><\/p>\n\n<div class=\"pmpro\"><div class=\"pmpro_card pmpro_content_message\"><div class=\"pmpro_card_content\">Dieser Inhalt ist nur f\u00fcr Benutzer der Gruppe: Medizinische Fachperson zug\u00e4nglich <br \/><a href=\"https:\/\/medizinonline.com\/it\/il-mio-conto\/pacchetti\/\">Jetzt beitreten<\/a><\/div><div class=\"pmpro_card_actions pmpro_font-medium\">Already a member? <a href=\"https:\/\/medizinonline.com\/it\/effettuare-il-login\/?redirect_to=https%3A%2F%2Fmedizinonline.com%2Fit%2Fdati-a-lungo-termine-sui-modulatori-cftr-nei-bambini-con-fibrosi-cistica%2F\">Accedi<\/a><\/div><\/div><\/div>","protected":false},"excerpt":{"rendered":"<p>La fibrosi cistica (FC) \u00e8 una delle malattie metaboliche congenite pi\u00f9 comuni in Europa. Le opzioni di trattamento per le persone affette da FC sono aumentate in modo significativo negli&#8230;&hellip;... <\/p>\n<div class=\"pmpro\"><div class=\"pmpro_card pmpro_content_message\"><div class=\"pmpro_card_content\">Dieser Inhalt ist nur f\u00fcr Benutzer der Gruppe: Medizinische Fachperson zug\u00e4nglich <br \/><a href=\"https:\/\/medizinonline.com\/it\/il-mio-conto\/pacchetti\/\">Jetzt beitreten<\/a><\/div><div class=\"pmpro_card_actions pmpro_font-medium\">Already a member? <a href=\"https:\/\/medizinonline.com\/it\/effettuare-il-login\/?redirect_to=https%3A%2F%2Fmedizinonline.com%2Fit%2Fdati-a-lungo-termine-sui-modulatori-cftr-nei-bambini-con-fibrosi-cistica%2F\">Accedi<\/a><\/div><\/div><\/div>","protected":false},"author":7,"featured_media":410404,"comment_status":"closed","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"_acf_changed":false,"pmpro_default_level":"","cat_1_feature_home_top":false,"cat_2_editor_pick":false,"csco_eyebrow_text":"Rapporto di studio","footnotes":""},"category":[11519,11306,11443,11468,11550,11515],"tags":[15506,83265,21483,83264,12189,83267],"powerkit_post_featured":[],"class_list":["post-410403","post","type-post","status-publish","format-standard","has-post-thumbnail","category-formazione-continua","category-medicina-interna-generale","category-pediatria-it","category-pneumologia","category-rx-it","category-studi","tag-cf-it","tag-elexacaftor-it","tag-fibrosi-cistica-it-2","tag-ivacaftor-it","tag-modulatori-cftr","tag-tezacaftor-it","pmpro-level-required","pmpro-level-1","pmpro-no-access"],"acf":[],"publishpress_future_action":{"enabled":false,"date":"2026-04-11 10:16:59","action":"change-status","newStatus":"draft","terms":[],"taxonomy":"category","extraData":[]},"publishpress_future_workflow_manual_trigger":{"enabledWorkflows":[]},"wpml_current_locale":"it_IT","wpml_translations":{"pt_PT":{"locale":"pt_PT","id":410329,"slug":"dados-a-longo-prazo-sobre-os-moduladores-cftr-em-criancas-com-fibrose-quistica","post_title":"Dados a longo prazo sobre os moduladores CFTR em crian\u00e7as com fibrose qu\u00edstica","href":"https:\/\/medizinonline.com\/pt-pt\/dados-a-longo-prazo-sobre-os-moduladores-cftr-em-criancas-com-fibrose-quistica\/"},"es_ES":{"locale":"es_ES","id":410340,"slug":"datos-a-largo-plazo-sobre-los-moduladores-del-cftr-en-ninos-con-fibrosis-quistica","post_title":"Datos a largo plazo sobre los moduladores del CFTR en ni\u00f1os con fibrosis qu\u00edstica","href":"https:\/\/medizinonline.com\/es\/datos-a-largo-plazo-sobre-los-moduladores-del-cftr-en-ninos-con-fibrosis-quistica\/"}},"_links":{"self":[{"href":"https:\/\/medizinonline.com\/it\/wp-json\/wp\/v2\/posts\/410403","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/medizinonline.com\/it\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/medizinonline.com\/it\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/medizinonline.com\/it\/wp-json\/wp\/v2\/users\/7"}],"replies":[{"embeddable":true,"href":"https:\/\/medizinonline.com\/it\/wp-json\/wp\/v2\/comments?post=410403"}],"version-history":[{"count":1,"href":"https:\/\/medizinonline.com\/it\/wp-json\/wp\/v2\/posts\/410403\/revisions"}],"predecessor-version":[{"id":410405,"href":"https:\/\/medizinonline.com\/it\/wp-json\/wp\/v2\/posts\/410403\/revisions\/410405"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/medizinonline.com\/it\/wp-json\/wp\/v2\/media\/410404"}],"wp:attachment":[{"href":"https:\/\/medizinonline.com\/it\/wp-json\/wp\/v2\/media?parent=410403"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/medizinonline.com\/it\/wp-json\/wp\/v2\/category?post=410403"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/medizinonline.com\/it\/wp-json\/wp\/v2\/tags?post=410403"},{"taxonomy":"powerkit_post_featured","embeddable":true,"href":"https:\/\/medizinonline.com\/it\/wp-json\/wp\/v2\/powerkit_post_featured?post=410403"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}