{"id":410329,"date":"2025-11-20T00:30:00","date_gmt":"2025-11-19T23:30:00","guid":{"rendered":"https:\/\/medizinonline.com\/?p=410329"},"modified":"2025-10-23T14:41:36","modified_gmt":"2025-10-23T12:41:36","slug":"dados-a-longo-prazo-sobre-os-moduladores-cftr-em-criancas-com-fibrose-quistica","status":"publish","type":"post","link":"https:\/\/medizinonline.com\/pt-pt\/dados-a-longo-prazo-sobre-os-moduladores-cftr-em-criancas-com-fibrose-quistica\/","title":{"rendered":"Dados a longo prazo sobre os moduladores CFTR em crian\u00e7as com fibrose qu\u00edstica"},"content":{"rendered":"\n<p><strong>A fibrose qu\u00edstica (FC) \u00e9 uma das doen\u00e7as metab\u00f3licas cong\u00e9nitas mais comuns na Europa. As op\u00e7\u00f5es de tratamento para as pessoas que sofrem de FC expandiram-se significativamente nos \u00faltimos anos. Os moduladores da CFTR melhoram a fun\u00e7\u00e3o da prote\u00edna CFTR defeituosa e s\u00e3o, por conseguinte, os primeiros medicamentos com um efeito causal, pelo menos parcial, na FC. Num estudo de extens\u00e3o aberto de fase IIIb, a utiliza\u00e7\u00e3o da terapia combinada de ivacaftor, elexacaftor e tezacaftor foi investigada em crian\u00e7as de 6-11 anos de idade durante um per\u00edodo de 96 semanas.   <\/strong><\/p>\n\n<div class=\"pmpro\"><div class=\"pmpro_card pmpro_content_message\"><div class=\"pmpro_card_content\">Dieser Inhalt ist nur f\u00fcr Benutzer der Gruppe: Medizinische Fachperson zug\u00e4nglich <br \/><a href=\"https:\/\/medizinonline.com\/pt-pt\/a-minha-conta\/pacotes\/\">Jetzt beitreten<\/a><\/div><div class=\"pmpro_card_actions pmpro_font-medium\">Already a member? <a href=\"https:\/\/medizinonline.com\/pt-pt\/iniciar-sessao\/?redirect_to=https%3A%2F%2Fmedizinonline.com%2Fpt-pt%2Fdados-a-longo-prazo-sobre-os-moduladores-cftr-em-criancas-com-fibrose-quistica%2F\">Log in here<\/a><\/div><\/div><\/div>","protected":false},"excerpt":{"rendered":"<p>A fibrose qu\u00edstica (FC) \u00e9 uma das doen\u00e7as metab\u00f3licas cong\u00e9nitas mais comuns na Europa. As op\u00e7\u00f5es de tratamento para as pessoas que sofrem de FC expandiram-se significativamente nos \u00faltimos anos&#8230;.&hellip;... <\/p>\n<div class=\"pmpro\"><div class=\"pmpro_card pmpro_content_message\"><div class=\"pmpro_card_content\">Dieser Inhalt ist nur f\u00fcr Benutzer der Gruppe: Medizinische Fachperson zug\u00e4nglich <br \/><a href=\"https:\/\/medizinonline.com\/pt-pt\/a-minha-conta\/pacotes\/\">Jetzt beitreten<\/a><\/div><div class=\"pmpro_card_actions pmpro_font-medium\">Already a member? <a href=\"https:\/\/medizinonline.com\/pt-pt\/iniciar-sessao\/?redirect_to=https%3A%2F%2Fmedizinonline.com%2Fpt-pt%2Fdados-a-longo-prazo-sobre-os-moduladores-cftr-em-criancas-com-fibrose-quistica%2F\">Log in here<\/a><\/div><\/div><\/div>","protected":false},"author":7,"featured_media":410331,"comment_status":"closed","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"_acf_changed":false,"pmpro_default_level":"","cat_1_feature_home_top":false,"cat_2_editor_pick":false,"csco_eyebrow_text":"Relat\u00f3rio do estudo","footnotes":""},"category":[11521,11524,11305,11450,11547,11551],"tags":[15514,83351,21489,83349,12203,83353],"powerkit_post_featured":[],"class_list":["post-410329","post","type-post","status-publish","format-standard","has-post-thumbnail","category-estudos","category-formacao-continua","category-medicina-interna-geral","category-pediatria-pt-pt","category-pneumologia-pt-pt","category-rx-pt","tag-cf-pt-pt","tag-elexacaftor-pt-pt","tag-fibrose-cistica-pt-pt-2","tag-ivacaftor-pt-pt","tag-moduladores-cftr","tag-tezacaftor-pt-pt","pmpro-level-required","pmpro-level-1","pmpro-no-access"],"acf":[],"publishpress_future_action":{"enabled":false,"date":"2026-05-04 05:55:00","action":"change-status","newStatus":"draft","terms":[],"taxonomy":"category","extraData":[]},"publishpress_future_workflow_manual_trigger":{"enabledWorkflows":[]},"wpml_current_locale":"pt_PT","wpml_translations":{"es_ES":{"locale":"es_ES","id":410340,"slug":"datos-a-largo-plazo-sobre-los-moduladores-del-cftr-en-ninos-con-fibrosis-quistica","post_title":"Datos a largo plazo sobre los moduladores del CFTR en ni\u00f1os con fibrosis qu\u00edstica","href":"https:\/\/medizinonline.com\/es\/datos-a-largo-plazo-sobre-los-moduladores-del-cftr-en-ninos-con-fibrosis-quistica\/"}},"_links":{"self":[{"href":"https:\/\/medizinonline.com\/pt-pt\/wp-json\/wp\/v2\/posts\/410329","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/medizinonline.com\/pt-pt\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/medizinonline.com\/pt-pt\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/medizinonline.com\/pt-pt\/wp-json\/wp\/v2\/users\/7"}],"replies":[{"embeddable":true,"href":"https:\/\/medizinonline.com\/pt-pt\/wp-json\/wp\/v2\/comments?post=410329"}],"version-history":[{"count":1,"href":"https:\/\/medizinonline.com\/pt-pt\/wp-json\/wp\/v2\/posts\/410329\/revisions"}],"predecessor-version":[{"id":410333,"href":"https:\/\/medizinonline.com\/pt-pt\/wp-json\/wp\/v2\/posts\/410329\/revisions\/410333"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/medizinonline.com\/pt-pt\/wp-json\/wp\/v2\/media\/410331"}],"wp:attachment":[{"href":"https:\/\/medizinonline.com\/pt-pt\/wp-json\/wp\/v2\/media?parent=410329"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/medizinonline.com\/pt-pt\/wp-json\/wp\/v2\/category?post=410329"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/medizinonline.com\/pt-pt\/wp-json\/wp\/v2\/tags?post=410329"},{"taxonomy":"powerkit_post_featured","embeddable":true,"href":"https:\/\/medizinonline.com\/pt-pt\/wp-json\/wp\/v2\/powerkit_post_featured?post=410329"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}