This content is machine translated Disease-modifying therapies for ATTR-CM TTR stabilizers, gene silencing and gene scissors: where do we stand? Advances in the understanding of the pathophysiology of transthyretin amyloid cardiomyopathy (ATTR-CM) have revolutionized the therapeutic landscape in recent years. TTR stabilizers such as tafamidis and acoramidis can reduce TTR...…
View Post 4 min This content is machine translated Rare diseases: hATTR amyloidosis What treatment options are available today? Transthyretin-associated amyloidosis (ATTR) is hereditary (hATTR) or acquired (wATTR). In patients with unclear left ventricular hypertrophy and characteristic findings, it is recommended to investigate the presence of cardiac amyloidosis. In…
